Q&A: Families shouldn’t have to coordinate Sweden’s rare disease care

A Q&A with Zozan Sewger Kvist, CEO of rare disease competence center Ågrenska, on stalled reform, uneven access to care in Europe and the limits of regulation.

POLITICO

Dysfunction in the homeostasis of iron and other elements likely contributes to the development of Parkinson's disease (PD), and Dr. Paul Lingor is working to identify patterns of bioelements in CSF that could be used as biomarkers. He is also studying tear fluid as a potential biomarker source and is involved in studying PD therapies, including the drug Fasudil as well as combinations of advanced therapies for people with later-stage PD. Learn more about his work in our latest podcast episode!

https://www.michaeljfox.org/podcast/episode-20-studying-csf-element-profiles-and-tear-fluid-potential-biomarkers-and-novel-and

#Parkinsons #ParkinsonsDisease #ParkinsonsResearch #Neuroscience #Neurology #Biomarkers #Biomarker #Diagnostics #ClinicalTrials #AdvancedTherapies #Research #MJFF

Episode 20: Studying CSF Element Profiles and Tear Fluid as Potential Biomarkers, and Novel and Combined Therapies for PD with Paul Lingor

Dr. Paul Lingor discusses his work in this area to identify patterns of bioelements in CSF that could serve as Parkinson's disease biomarkers.

The Michael J. Fox Foundation for Parkinson's Research | Parkinson's Disease

NSW Health, Australia, has set a national benchmark for standardising the preparation of pharmaceuticals and advanced therapeutic products with a new Policy Directive that outlines new and updated state-wide approaches.

Learn more about the Directive & author Kerry Watts: https://www.medicalresearch.nsw.gov.au/future-proofing-nsw-health-production-ofpharmaceuticals-and-advanced-therapeutics/ #AdvancedTherapies #CellTherapies #GeneTherapies

NexCAR19 CAR T Cell Therapy: Tailoring the Approach to B-Cell Lymphoma Treatment

NexCAR19 CAR T cell therapy is a groundbreaking treatment for B-cell lymphomas that has recently received approval in India. This innovative therapy harnesses the power of the patient's own immune system to fight cancer cells. #NexCAR19 #oncologyhealthcareindia #carttherapy #india #immunoactindia #lymphoma #advancedtherapies

https://mindfulcells.com/2023/12/nexcar19-car-t-cell-therapy-tailoring-the-approach/

#science #scientist #biology #mentalhealth

What Makes NexCAR19 CAR T Cell Therapy Unique? Find Out Here

The power of technology: NexCAR19 CAR T Cell therapy, approved by CDSCO in India. Discover its influence on CD4+ and CD8+ T cell subsets. #CARTCellTherapy #NexCAR19 #NexCAR19CARTCelltherapy #OncologyhealthcareIndia #Regenerativehealtheducation #ActalyCel™ #Actalycabtageneautoleucel

Mindfulcells
3rd ARRIGE Albrecht Müller Seminar (free online conference) on ‘Human Therapeutic Applications of Gene Editing’ November 13th, 2023 – 2pm-5pm (CET) – Paris time.
#CRISPR #GenomeEditing #ClinicalTrials #BaseEditing #primeediting #crisprcas9 #genetherapy #advancedtherapies #ARRIGE #ResponsibleResearch #ethics #bioethics #rri #innovation
Full information and registrarion link to gain free access to this meeting available at:
https://www.arrige.org/portfolio/3rd-albrecht-muller-arrige-seminar/
3rd Albrecht Müller ARRIGE Seminar – ARRIGE

What single market? Why Romanians get new medicines 2 years after Germans

Not all patients are equal when it comes to treatment with cutting-edge drugs.

POLITICO
Why Big Pharma might think twice about running away to America

A major drug pricing crackdown in the US is threatening drug companies’ bottom lines.

POLITICO
TDT: rare disease has big impact on patients, families and society

What is transfusion-dependent beta thalassemia and how could we improve the lives of those impacted?

POLITICO
EU pharma reform: Winners and losers

The Commission has published its first major overhaul to the bloc’s medicines regulations in 20 years.

POLITICO
EU transparency commissioner: No conflict of interest for Ursula von der Leyen’s husband

Green lawmakers had raised concerns about Heiko von der Leyen’s role in a biotech company that received EU funds.

POLITICO