Catherine Collingwood EstesSep 25, 2024
#PBM leadership: "We're going to look for as many #OrphanDrug situations as we can so that we can extend our patents and keep #profits high." #FixedItForYou #Prescriptions https://www.axios.com/2024/09/25/old-drugs-repurposed-rare-diseases
AI's latest trick: repurposing old drugs for rare disease

A new AI tool can identify candidates for 17,000 conditions — the largest number of diseases that any single AI model can handle to date.

Axios
Alan KotokSep 12, 2023

A new company developing treatments for neurological and psychiatric diseases from aberrant immune system activity is raising $58 million in seed funds.

https://sciencebusiness.technewslit.com/?p=45199

#News #Press #Science #Business #Biotechnology #Finance #Autoimmune #Encephalitis #MentalHealth #Psychosis #SeedFunds #VentureCapital #Investment #Preclinical #FDA #OrphanDrug #RareDisease

Autoimmune Neuro Disease Start-Up Raises $58M

A new company developing treatments for neurological and psychiatric diseases from aberrant immune system activity is raising $58 million in seed funds.

Science and Enterprise
IQWiGJan 17, 2023

#Pressemitteilung

#Vutrisiran bei hereditärer Transthyretin-Amyloidose: Anhaltspunkt für geringen Zusatznutzen

Der Hersteller hat die reguläre frühe Nutzenbewertung für sein #OrphanDrug vorgezogen, was seit 2019 möglich ist. Weniger vielversprechende neue Wirkstoffe profitieren weiterhin von der Zusatznutzenfiktion.