Yan Leyfman, MDMIT researchers have developed a novel tool, called PASTE, that can insert large gene sequences where they want in the genome. This approach can be used to treat cystic fibrosis & Leber congenital amaurosis.
https://www.nature.com/articles/s41587-022-01527-4
#genetherapy #geneediting #geneticmutations #geneticcorrection #crispr
