Update on future #treatments for #PKU

From the NSPKU conference held May 2024 here are my notes from the sessions on #sepiapterin, #mRNA, #gene #therapy, solute carrier 6, and oral options for #PegPal / #Palynziq

https://buff.ly/4awqcJP

#LivingWithPKU #RareDisease #phenylketonuria #PCU

Day One of the #PKUGlobe23 Conference on #ScientificProgress was fascinating. Many thanks to the speakers!

Sadly, missed day two, but looking forward to day three on the patient experience -> https://gener8.eventsair.com/pkuglobe23/
#Sepiapterin #SLC6A19Blockers #CRISPRGeneEditing #mRNATherapy #LivingWithPKU #PKU