poconnorMay 24, 2024

Update on future #treatments for #PKU

From the NSPKU conference held May 2024 here are my notes from the sessions on #sepiapterin, #mRNA, #gene #therapy, solute carrier 6, and oral options for #PegPal / #Palynziq

https://buff.ly/4awqcJP

#LivingWithPKU #RareDisease #phenylketonuria #PCU

PKU future treatments update. Sepiapterin, mRNA, gene therapy

The NSPKU conference held from 17-19 May 2024 included an update on possible new treatments for PKU. These are my notes from the sessions on sepiapterin, mRNA, gene therapy, solute carrier 6, and options for PegPal.

Pig Pen