ABC Feeds5d ago

It's $2.5m a dose and it's giving some children another chance at life
By Janelle Miles

Children born with a rare neuromuscular disorder are being given another chance in life thanks to a new treatment experts are calling a "game-changer".

https://www.abc.net.au/news/2026-03-31/qld-gene-therapy-giving-children-another-chance/106486714

#Geneticdisorders #InfantHealth #PublicHealth #JanelleMiles

After treatment on her first day of life, Willow’s first steps are a medical triumph

Children born with a rare neuromuscular disorder are being given another chance in life thanks to a new treatment experts are calling a "game-changer".