Carolyn Barber, MDFeb 5, 2023

CRISPR—a magic eraser!

A patient who lived with hereditary angioedema for decades received an experimental gene-editing therapy that’s changed her life. 

“It's like living with a new body again really because...the options are unlimited now."

Bonus: she’s off her meds,too!👏

https://bit.ly/3YqUmIR

#medicine #genetx #geneticmutations #crispr #medtwitter

Ground-breaking gene-editing treatment leaves patient feeling like they have 'a new body'

Being given a whole new body might sound like something from a sci-fi movie but a New Zealander says a new genetic treatment has felt just like that.

RNZ
Show threadYan Leyfman, MDDec 21, 2022
#cancerawareness #cancerawarenessmonth #cancer #oncology #immunotherapy #CARTcells #genetherapy #cartcellrx #medicine #celltherapy #tcellrx #CART #genetx #chernobyl #patient #chernobylsurvivor #patientadvocate #patientnavigator #genetherapy #geneticengineering #advocate #advocacy #patientcare #together #patientsupport #cancercoalition #cancerresearch #chernobyl #survivor #caretaker #personalizedmedicine #cancer #oncology #growth #medicine
Carolyn Barber, MDDec 14, 2022
In mice with uncontrolled epilepsy, researchers have designed a new gene therapy that helped prevent seizures and ⬆️ their chances of survival. https://bit.ly/3iXcAlL @macquarie_Uni @mq_drc #genetx #epilepsy
Gene therapy offers hope for severe epilepsy

A study published this month in Science Advances by a team of researchers at Macquarie University's Dementia Research Center showed their treatment could prevent seizures in mice by clearing build‑ups of a protein in the brain.

Medical Xpress
Show threadYan Leyfman, MDNov 12, 2022
#immunotherapy #CARTcells #genetherapy #cartcellrx #medicine #celltherapy #tcellrx #CART #genetx #chernobyl #patient #chernobylsurvivor #patientadvocate #patientnavigator #genetherapy #geneticengineering #crispr #cellulartherapeutics #LLMCongress2022 #healthcare #success #innovation #research #grateful #growth #mentorship #msc #msctherapy #stemcell #stemcells #stemcellrx