MediPaCeMar 1, 2023

"What we need is a #PublicPrivatePartnership approach, because the current drug development model does not work in the case of #UltraRareDiseases"

➡️See Nick Sireau's full interview:
https://www.youtube.com/watch?v=RKzwBmUYKF4

➡️Read the full article about overcoming challenges in #PatientEngagement in the #RareDiseaseCommunity: https://medipace.com/2023/02/28/raredisease-community/

#PatientEngagement #RareDiseaseDay

#RareDiseaseDay: Overcoming challenges to patient engagement in the rare disease community

YouTube
Poetry NewsDec 20, 2022

Creating drugs for
Ultrarare diseases
Is the hard part now

#science #drugs #ultrararediseases #haiku #poetry

https://www.nytimes.com/2022/12/19/health/rare-disease-genetic-treatments.html

They Created a Drug for Susannah. What About Millions of Other Patients?

Scientists have made rapid progress in customizing drugs for ultrarare diseases. The hard part now is making such treatments on a large scale.