Front PageThey thought their son lived an isolated life. But when he died, friends showed up in droves.
https://fed.brid.gy/r/https://www.upworthy.com/mats-steen-ibelin-world-of-warcraft-ex1
untsúkonpìiūI followed #WVE for some time now. I subscribed its SEC filing and news rss to the firsthand message. So yesterday the company announced their positive clinical result for #DuchenneMuscularDystrophy. When I got that news, I immediately bought in the stock pre-market at around $6.74. Made some 50% nice profit. Have free cash to buy a new iPad air now. 🙂
Gunning GroupThrilled to share our story on the first rationally designed #covalent #HDAC inhibitor! YSR734 uses an SNAr-reactive electrophile to engage a noncatalytic nitrosylation site cysteine in #HDAC2, showing in vitro activity in AML & #DuchenneMuscularDystrophy!
https://pubs.acs.org/doi/10.1021/acs.jmedchem.3c01236
https://pubs.acs.org/doi/10.1021/acs.jmedchem.3c01236
EMBO Mol. MedicineA. Jayaraman and S. Pettersson discuss the studies by Farini et al & Kalkan et al @EmboMolMed, that independently reported the potential role of the #GutMicrobiota in the pathogenesis of #DuchenneMuscularDystrophy.
N&V 🗞️: https://doi.org/10.15252/emmm.202217324
👉 Full articles #openaccess:
https://doi.org/10.15252/emmm.202216225
https://doi.org/10.15252/emmm.202216244
Alan KotokData Support Placebo Group Alternatives in Rare Disease Trials
Findings from a review of medical #data and #records indicate matched #genetic control groups may not be needed in clinical trials testing treatments for Duchenne muscular dystrophy.
https://sciencebusiness.technewslit.com/?p=44426
#News #Science #Business #ClinicalTrials #DuchenneMuscularDystrophy #Neuroscience #Neurology #ControlGroup #Placebo #Statistics #RareDisease #InheritedDisease #RealWorldData
Nicki LygoHuge thanks @ElectricWill for your wonderful donation 🙌🏻 to our fundraising campaign for #DuchenneMuscularDystrophy
I’m really looking forward to connecting with you more on here!
Jane@DrLygo I didn’t know they were close to finding a cure. I known 2 families afflicted by #duchennemusculardystrophy and it’s just heartbreaking. Well done to your young man.
Our family has a young friend with #DuchenneMuscularDystrophy. We fundraise to help find a cure, - currently believed to be imminent enough to save many thousands of lives.
Each of my children has taken on a challenge to help. Last year, my 11 year-old walked the 102 mile #CotswoldWay. Thanks to people’s incredible generosity, he raised £10k for #DuchenneUK!
I am so proud of him ❤️
I would be so grateful if you could boost this to help us raise awareness. Thank you!
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